Advancing the health of children by turning scientific discovery into medical innovation.
The European Research Infrastructure for Translational Medicine #EU_RI.
Supporting research communities translate scientific discoveries into #patient benefit.
The European Platform for Medicines Repurposing. Funded by #HorizonEurope.
remedi4all.org
Nonprofit that funds clinical trials testing approved therapies. Our patient-focused, disease-agnostic approach focuses on clinical evidence to de-risk and catalyze follow-on funding to build clinical evidence for regulatory approval or off-label use.
Lecturer Researcher Advocate
#PKU #LowProtein #BrainHealth #RareDisease
"NΓ neart go cur le chΓ©ile"
The views and opinions expressed here are solely my own
HRB-funded clinical trial network aiming to increase the quantity and quality of rare disease clinical trials in Ireland, keeping the patient voice at our core.
Interested in all things healthcare science-y, slightly obsessed with mitochondria. Digital Health Innovation Lead @FutureNeuro_ie. All views my own.
Health equality advocate. Animals, Art, Anthropology. Living in Dublin, working at Retina International. Views my own.
FutureNeuro is the Research Ireland Centre for Translational Brain Science, based in RCSI University of Medicine and Health Sciences. Our vision is to change the patient journey for people affected by brain conditions.
In4kids is a national clinical trial network funded by Health Research Board that supports researchers in Ireland to deliver high-quality clinical trials.
Paediatrician
Dublin Ireland
CIRM's mission is to accelerate world-class science to deliver transformative regenerative medicine treatments in an equitable manner to a diverse California and world. Visit our website at cirm.ca.gov.
The official CIRM account.
Advancing knowledge, awareness, and education leading to the discovery and clinical application of genetic and cellular therapies to alleviate human disease.
The European Reference Network for Rare Hereditary Metabolic Disorders (MetabERN). A better future for Rare Inherited Metabolic Disease patients.
Visit us π https://metab.ern-net.eu/
Combining frontier AI & frontier biology to help scientists cure or prevent disease
Neuroscientist turned gene editor!
Postdoc in the Ahrens-Nicklas & Musunuru labs | Neuroscience PhD from Penn, Korb lab | Barnard College alum | she/her
Senior Director and Staff Scientist at Denali Therapeutics. My lab is focused on understanding how lysosomal function is perturbed in Parkinson's disease and LSDs.
The Telethon Institute of Genetics and Medicine (TIGEM) is a Telethon Foundation research center located in Pozzuoli (Italy) that aims to help people with rare genetic disorders across the world.
CEO, Health Research Charities Ireland @hrci.bsky.social (views own). PhD in genetics. Ambitious for a better world through collaboration & inclusion. She/Her
π€ΉββοΈ PPI | research impact | health data | evidence-based policy | genomics | rare diseases...