Efficient EGFP reporter transgene delivery to NHP T cells by LNP. Next step is delivering the CAR in vivo
#ESGCT2025 #InVivoCART
Cecilia Cotta-Ramusino
@TesseraTx
08.10.2025 10:29 — 👍 1 🔁 0 💬 0 📌 0
Liver directed Klotho overexpression fails to protect from ALS in mice
Sergi Verdes, Universitat Autonoma de Barcelona
#ALS #GeneTherapy #Klotho
07.10.2025 18:45 — 👍 1 🔁 0 💬 0 📌 0
Official press release for @sonothera.bsky.social presentation @ #ESGCT2025.
Results show high levels of durable human dystrophin protein expression exceeding
50% of endogenous levels have been achieved in NHP.
Poster Session 2, Oct 9th. Poster P0266.
#Dmd #GeneTherapy #nonviral
07.10.2025 18:39 — 👍 2 🔁 0 💬 0 📌 0
Executive, NED | Strategy, Leadership, Advocacy | Industry-Academia-Gov | Deputy Director, Australian Regenerative Medicine Institute | DEI, STEM Workforce | Consultant, Career Coach | she/her | #Wurundjeri #Australia
physician-scientist, author, editor
https://www.scripps.edu/faculty/topol/
Ground Truths https://erictopol.substack.com
SUPER AGERS https://www.simonandschuster.com/books/Super-Agers/Eric-Topol/9781668067666
Senior Advisor, therapeutic gene editing at Eli Lilly. Previously Spark Tx, Rice University. Thoughts and opinions my own
Our mission is to enable the promise of genomics to better human health by creating the world’s most advanced sequencing technologies.
Genome Editor. Co-developer of Easi-CRISPR; http://bit.ly/Easi-CRISPR. World now needs peace and solidarity, not war. Opinions mine.
Clinic-minded genome + epigenome editor. Professor of Molecular Therapeutics, UC Berkeley. Director for Technology and Translation, Innovative Genomics Institute, ibid.
Beatles fan.
Art work credit: Fyodor Vasiliev "A Meadow in the Rain" (1872).
Chief Scientific Strategist, Gladstone-UCSF Institute of Genomic Immunology.
Former Cell editor.
Genetics, genomics, immunology, oceanology, mixology, always collecting new -ologies.
Epigeneticist, Scientist & Molecular Biologist studying epigenetic cellular memory, epigenetic inheritance & mechano-epigenomic code in gliomas.
#epigenomics #epigenetics #singlecell #chromatin
https://www.linkedin.com/in/damian-toczydlowski/
AAV Gene therapy researcher + below average ultrarunner. 2022 ASGCT CDA. 2023-2028 CFF postdoc to faculty grant. Thomas Lab
RNA and programmable nuclease innovator 🧬 | R&D leader in amplification-free molecular detection systems ⚙️ | Consulting to bridge enzyme science, business & strategy 🧪 | Amateur bulldog whisperer 🦴
Academic. Interested in Physiology, Haemophilia & Related Bleeding Disorders, Patient Advocacy, Gene Therapy, Clinical Trials, Pharmacovigilance
Cardiologist, geneticist, and gene editor. Author of #TheCRISPRGeneration and #GenomeEditingAPracticalGuide
We develop and apply advanced genetic manipulation technologies to make sense of biological complexity. Formerly @Genentech now @umontreal.ca. More about our lab and research here: labohaley.com
Vice Chair of Hematology. Director of Blood Marrow and Transplantation and Cellular Therapies.@MayoClinic @MayoCancerCare
Views are my own.
Nucleic acid delivery, nanoparticles, gene therapy and occasionally wildlife photography.
The longest running international CRISPR conference, established in 2008. CRISPR 2025 will be held from February 16-20, 2025 in Christchurch, New Zealand.
https://www.crispr2025.org/
Developmental Geneticist (mice & worms)
RNA biology, gene editing, gene delivery
Director @ Vertex | cell and gene therapies
Business leader in genomics and molecular diagnostics, partnering to advance healthcare innovation, concert goer 🎶, trail exlporer 🏔️, recipe tweaker 🍳. Opinions my own.
Doctor. Scientist. Sickle Cell Disease.
Biomedical Science in Africa.
CHARTA - Coordination, Health, Advocacy, Research, Training in Africa
